D.S.K. has received honoraria for advisory board participation from Biogen, Roche and Novartis, and speaker’s fees from Biogen, Novartis and Roche. M.A.F. is a site principal investigator for Roche and Novartis Gene Therapies Inc. clinical trials, and their institution has received funds for contract research related to the conduct of these trials. M.A.F. has received honoraria for advisory board participation from Biogen, Novartis and Roche, and has received speaker’s fees from Biogen, Roche and Novartis. G.B. has participated in clinical trials sponsored by Roche, Novartis, Sarepta, Pfizer, NS Pharma, ReveraGen and Scholar Rock, and has received speaker and/or consulting fees from Sarepta, PTC Therapeutics, Pfizer, Biogen, Novartis Gene Therapies Inc. (AveXis) and Roche, and grants from Sarepta, Roche and Novartis Gene Therapies Inc.