Elamipretide: First Approval

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Stealth BioTherapeutics. FDA grants Rare Pediatric Disease designation to Stealth BioTherapeutics for elamipretide for the treatment of Barth syndrome [media release]. 03 Mar 2020. https://stealthbt.com/.

Stealth BioTherapeutics. Stealth BioTherapeutics granted Orphan Drug designation of elamipretide for treatment of Leber’s hereditary optic neuropathy [media release]. 30 Apr 2018. https://stealthbt.com/.

Stealth BioTherapeutics. Stealth BioTherapeutics receives Orphan Drug designation from the European Medicines Agency for elamipretide for the treatment of Barth syndrome [media release]. 01 Jun 2021. https://stealthbt.com/.

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Stealth BioTherapeutics. Stealth BioTherapeutics granted Orphan Drug designation of elamipretide for treatment of patients with primary mitochondrial myopathy [media release]. 02 Oct 2017. https://stealthbt.com/.

Stealth BioTherapeutics. Stealth BioTherapeutics receives Orphan Drug designation from the European Medicines Agency for elamipretide for the treatment of myopathic mitochondrial DNA depletion syndrome [media release]. 31 May 2022. https://stealthbt.com/.

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Stealth BioTherapeutics. Stealth BioTherapeutics enters into exclusive licensing agreement with Pharmanovia to commercialize elamipretide for the treatment of Barth syndrome in Europe and key global territories [media release]. 30 May 2023. https://stealthbt.com/.

Stealth BioTherapeutics. Stealth BioTherapeutics strengthens IP portfolio with issuance of U.S. patents covering elamipretide for Barth syndrome [media release]. 23 Aug 2021. https://stealthbt.com/.

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